Full Schedule

8:00 AM - 9:00 AM ET

Attendee Breakfast

Location: Atlantic Prefunction - Level 3

8:30 AM - 5:30 PM ET

Speaker Ready Room

Location: 253C

8:30 AM - 7:30 PM ET

Registration Open

Location: Level 2 Prefunction - East Building

9:30 AM - 11:00 AM ET

Special Symposium: Advancing Biomarkers in Sickle Cell Disease: Regulatory Pathways, Clinical Integration & Patient-Centered Endpoints

Location: Atlantic D

Chair: – Albert Einstein College of Medicine, Bronx, NY, USA

Sponsored By

9:30 AM - 11:00 AM ET

Special Symposium: Advancing Biomarkers in Sickle Cell Disease: Regulatory Pathways, Clinical Integration & Patient-Centered Endpoint

Location: Atlantic D

Chair: – Albert Einstein College of Medicine, Bronx, NY, USA

9:30 AM - 9:35 AM ET

Welcome & Opening Remarks

Location: Atlantic D

Chair: – Albert Einstein College of Medicine, Bronx, NY, USA

9:35 AM - 9:45 AM ET

Biomarkers as Endpoints in Sickle Cell Disease: What Are They and Why Are They Important?

Location: Atlantic D

Speaker: – Wayne State University School of Medicine, Detroit, MI, USA

9:45 AM - 10:00 AM ET

FDA 101: Pathways to Biomarker Qualification & Approval

Location: Atlantic D

Speaker: – US FDA

10:00 AM - 10:10 AM ET

Patient-Centered Endpoints in Sickle Cell Disease

Location: Atlantic D

Speaker: – Cleveland Clinic

10:10 AM - 10:20 AM ET

Chronic Pain as a Clinical Trial Endpoint in Sickle Cell Disease

Location: Atlantic D

Speaker: – Virginia Commonwealth University

10:20 AM - 10:40 AM ET

Industry Sponsor Perspectives Panel

Location: Atlantic D

Moderator: – CSL Behring

Speaker: – Agios Pharmaceuticals

Speaker: – Novo Nordisk Inc.

Speaker: – Fulcrum Therapeutics, Cambridge, MA, USA

10:40 AM - 10:55 AM ET

Panel Discussion & Audience Q&A

Location: Atlantic D

10:55 AM - 11:00 AM ET

Closing Remarks

Location: Atlantic D

Chair: – Albert Einstein College of Medicine, Bronx, NY, USA

11:00 AM - 11:45 AM ET

Welcome Address: The State of Sickle Cell Disease in the Golden Age & Celebrating 20 Years of The Symposium

Location: Atlantic D

Speaker: – Foundation for Sickle Cell Disease Research

Speaker: – A-Rod Corp

Speaker: – Becker & Poliakoff

Speaker:

Speaker: – New Hope Missionary Baptist Church of Miami

Speaker:

Speaker: – The Bill & Melinda Gates Medical Research Institute (Gates MRI)

Speaker: – Fooundation for SIckle Cell Disease Research

Performer:

11:45 AM - 11:50 AM ET

Introduction to the Access to Care Keynote Presentation

Location: Atlantic D

Speaker: – South Florida Cardiology Consultants

11:50 AM - 12:45 PM ET

Access to Care Keynote Presentation: Research and Real-World Impact in Sickle Cell Disease

Location: Atlantic D

Presenter: – Florida Medicaid

Earn 1 CME Hour(s)

1:00 PM - 7:30 PM ET

Exhibit Hall Open

Location: Atlantic C

1:15 PM - 1:45 PM ET

Welcome Coffee Break in Exhibit Hall

Location: Atlantic C

1:45 PM - 3:15 PM ET

Historic Landmarks in Research and Care of Patients with Sickle Cell Disease

Location: Atlantic D

Chair: – Virginia Commonwealth University

Speaker: – Vanderbilt University Medical Center

Speaker: – Thomas Jefferson University

Earn 1.5 CME Hour(s)

1:45 PM - 2:05 PM ET

Milestones That Matter: The Evolution of Survival and Quality of Life in SCD

Location: Atlantic D

Speaker: – Thomas Jefferson University

2:05 PM - 2:25 PM ET

Rewriting Blood: The Genetic Reset of Sickle Cell Disease Through Hematopoietic Stem Cell Transplant

Location: Atlantic D

Panelist: – Vanderbilt University Medical Center

2:25 PM - 2:45 PM ET

Historical Landmarks in Pain Measurement and Care in Sickle Cell Disease

Location: Atlantic D

Speaker: – Virginia Commonwealth University

2:45 PM - 3:15 PM ET

Panel Discussion & Audience Q&A

Location: Atlantic D

3:15 PM - 3:20 PM ET

Break

3:20 PM - 4:20 PM ET

The Patient Symposium: Empowering Patients to Advance Sickle Cell Policy

Location: Atlantic D

Chair: – Sick Cells

Speaker:

Organizer: – Sick Cells

Earn 1 CME Hour(s)

4:20 PM - 4:50 PM ET

Break

4:50 PM - 6:15 PM ET

Investigational New Drug, Device and Therapeutics Symposium

Location: Atlantic D

Chair: – Wayne State University School of Medicine, Detroit, MI, USA

Panelist: – Novo Nordisk Inc.

Panelist: – Cellarity

Panelist: – CSL Behring

Panelist: – Sanofi

Panelist: – Beam Therapeutics

Panelist: – Agios Pharmaceuticals

Panelist: – Pfizer

4:50 PM - 4:55 PM ET

Chair Welcome

Location: Atlantic D

Chair: – Wayne State University School of Medicine, Detroit, MI, USA

4:55 PM - 5:30 PM ET

Company Introductions

Location: Atlantic D

Chair: – Wayne State University School of Medicine, Detroit, MI, USA

Panelist: – Novo Nordisk Inc.

Panelist: – Cellarity

Panelist: – Fulcrum Therapeutics, Cambridge, MA, USA

Panelist: – CSL Behring

Panelist: – Sanofi

Panelist: – Beam Therapeutics

Panelist: – Agios Pharmaceuticals

Panelist: – Pfizer

5:30 PM - 6:00 PM ET

Moderated Fireside Chat with the Panel

Location: Atlantic D

Chair: – Wayne State University School of Medicine, Detroit, MI, USA

Panelist: – Novo Nordisk Inc.

Panelist: – Cellarity

Panelist: – CSL Behring

Panelist: – Sanofi

Panelist: – Beam Therapeutics

Panelist: – Agios Pharmaceuticals

Panelist: – Pfizer

6:00 PM - 6:15 PM ET

Open Q&A with the Audience

Location: Atlantic D

Chair: – Wayne State University School of Medicine, Detroit, MI, USA

Panelist: – Novo Nordisk Inc.

Panelist: – Cellarity

Panelist: – CSL Behring

Panelist: – Sanofi

Panelist: – Beam Therapeutics

Panelist: – Agios Pharmaceuticals

Panelist: – Pfizer

6:15 PM - 7:30 PM ET

Welcome Reception and Poster Session in Exhibit Hall

Location: Atlantic C

Sponsored By

7:30 PM - 9:30 PM ET

Hope in Action: An Inspiring Evening with Ryan Clark | Dinner Provided

Location: Atlantic D

Warrior Keynote Speaker:

Chair: – Foundation for Sickle Cell Disease Research

Co-Chair: – Crisis 2 Crown International Inc.

Speaker: